Patient characteristics and outcomes
| Patient | Age/Sex | | Donor type | Conditioning regimen | Stem cell (CD34 cells) dose per kg of recipient | Post-HSCT outcome |
|---|---|---|---|---|---|---|
| 1 | 3 mo/male | IFN-γ | Haplo | Flu/Treo/PTCy | 5 million | Graft rejection/alive |
| 2 | 5 years/male | IFN-γ | MFD | Flu/Treo/TT | 5 million | Graft rejection/dead |
| 3 | 3 years/female | IFN-γ | MSD | Flu/Treo/TT | 10 million | Complete donor chimerism/alive |
| 4 | 2.5 years/female | IFN-γ | Haplo | Flu/Treo/TT TCRαβ depletion | 10 million | Complete donor chimerism/alive |
| 1 | 6 years/male (second HSCT) | IFN-γ | Haplo | Flu/Treo/TT TCRαβ depletion | 10 million | Mixed chimerism—improved after graded whole blood DLI/alive |
| 5 | 5 years/male | IL-12 | MFD | Flu/Treo | 7 million | Complete donor chimerism/alive |
| 6 | 10 years/male | IL-12 | Haplo | Flu/Treo/2 Gy TBI/PTCy | 8 million | Complete donor chimerism/alive |
| 7 | 6 years/female | IL-12 | Haplo | Flu/Treo/PTCy | 8 million | Mixed chimerism—improved after graded whole blood DLI/alive |
| Patient | Age/Sex | | Donor type | Conditioning regimen | Stem cell (CD34 cells) dose per kg of recipient | Post-HSCT outcome |
|---|---|---|---|---|---|---|
| 1 | 3 mo/male | IFN-γ | Haplo | Flu/Treo/PTCy | 5 million | Graft rejection/alive |
| 2 | 5 years/male | IFN-γ | MFD | Flu/Treo/TT | 5 million | Graft rejection/dead |
| 3 | 3 years/female | IFN-γ | MSD | Flu/Treo/TT | 10 million | Complete donor chimerism/alive |
| 4 | 2.5 years/female | IFN-γ | Haplo | Flu/Treo/TT TCRαβ depletion | 10 million | Complete donor chimerism/alive |
| 1 | 6 years/male (second HSCT) | IFN-γ | Haplo | Flu/Treo/TT TCRαβ depletion | 10 million | Mixed chimerism—improved after graded whole blood DLI/alive |
| 5 | 5 years/male | IL-12 | MFD | Flu/Treo | 7 million | Complete donor chimerism/alive |
| 6 | 10 years/male | IL-12 | Haplo | Flu/Treo/2 Gy TBI/PTCy | 8 million | Complete donor chimerism/alive |
| 7 | 6 years/female | IL-12 | Haplo | Flu/Treo/PTCy | 8 million | Mixed chimerism—improved after graded whole blood DLI/alive |
MSD, matched sibling donor; TBI, total body irradiation.
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