Table 1.

Clinical presentations in 22q11.2DS compared to duplications on 22q11.2 and TBX1 variants

Clinical disorder22q11.2DS LCRA-D 3-Mb deletion 22q11.2DS LCRA-B 1.5-Mb deletion22q11.2DS duplicationTBX1 loss or gain of function
Frequency 1/2,150 1/1,600 Rare (∼10–15 families) 
Congenital problems: % affected 
 Thymic hypoplasia 70–80% 1–2%a 20–45% 
 Thymic aplasia <1% Not reported Not reported 
 Hypocalcemia 50–65% 2.8% 45% 
 Cardiac defects 60–85% 4–6% 56% 
 Craniofacial features 80–90% 12.7% 100% 
 Speech delay (GERDb70–90% 46% 33% 
Postnatal concerns: % affected 
 Immunological 
  Allergy 60% 25% Unknown 
  Autoimmunity 5–10% 2.3% Unknown 
  CD3+ T cell lymphopenia 60–70% 2.6% Unknown 
  Decreased class switch memory B cells 70% 25% Unknown 
  Low pneumococcal vaccine responses 39% 0% Unknown 
 Hypogammaglobulinemia 6% 10–20% Unknown 
  Neurological 
  Developmental delay 8–10% 45–50% 30% 
  Autism spectrum disorder 15–40% 20% 38%c 
  Schizophrenia 30–35% Protective 38%c 
  Disrupted blood–brain barrier Unknown Not reported Not reported 
Clinical disorder22q11.2DS LCRA-D 3-Mb deletion 22q11.2DS LCRA-B 1.5-Mb deletion22q11.2DS duplicationTBX1 loss or gain of function
Frequency 1/2,150 1/1,600 Rare (∼10–15 families) 
Congenital problems: % affected 
 Thymic hypoplasia 70–80% 1–2%a 20–45% 
 Thymic aplasia <1% Not reported Not reported 
 Hypocalcemia 50–65% 2.8% 45% 
 Cardiac defects 60–85% 4–6% 56% 
 Craniofacial features 80–90% 12.7% 100% 
 Speech delay (GERDb70–90% 46% 33% 
Postnatal concerns: % affected 
 Immunological 
  Allergy 60% 25% Unknown 
  Autoimmunity 5–10% 2.3% Unknown 
  CD3+ T cell lymphopenia 60–70% 2.6% Unknown 
  Decreased class switch memory B cells 70% 25% Unknown 
  Low pneumococcal vaccine responses 39% 0% Unknown 
 Hypogammaglobulinemia 6% 10–20% Unknown 
  Neurological 
  Developmental delay 8–10% 45–50% 30% 
  Autism spectrum disorder 15–40% 20% 38%c 
  Schizophrenia 30–35% Protective 38%c 
  Disrupted blood–brain barrier Unknown Not reported Not reported 
a

Reflects low peripheral T cells.

b

Gastroesophageal reflux disease.

c

Listed as combined psychiatric disorders.

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