Table 1.

Clinical data summary

PatientSexGenotypeOriginAge referralAge onsetReferenceMajor manifestationPathogens identifiedNoninfectious triggers
A.II.4 Female WT/p.A240V Europe 31 years 4 years (21) Necrotizing cellulitis; pathergy-like inflammation; pneumonia; lung abscesses None identified Minor trauma 
B.III.8 Male WT/p.E314X Middle East 6 years 1.5 years ​ Necrotizing cellulitis; skin abscesses; necrotizing panniculitis; pneumonia P. aeruginosa; Enterobacter spp. Vaccination 
C.II.3 Male WT/p.K247RfsX25 South America 16 years 0.5 years ​ Necrotizing cellulitis; skin abscesses; pyoderma gangrenosum; pneumonia P. aeruginosa; S. aureus; C. perfringens Vaccination; surgery 
D.II.3 Female WT/p.S351VfsX55 Europe 28 years 28 years ​ Necrotizing cellulitis; skin abscesses None identified Surgery 
E.II.8 Female WT/p.W148X Europe 41 years 15 years (22) Cellulitis; skin abscesses; chorioamnionitis; pyelonephritis Klebsiella spp.; Pseudomonas spp.; C. perfringens; E. coli Minor trauma 
F.II.3 Male WT/c.788G>A (predicted p.R263Q) North America 38 years 2 mo ​ Soft tissue abscesses; pyoderma gangrenosum; osteomyelitis; inflammatory bowel disease; pneumonia S. epidermidis Minor trauma; vaccination; surgery 
PatientSexGenotypeOriginAge referralAge onsetReferenceMajor manifestationPathogens identifiedNoninfectious triggers
A.II.4 Female WT/p.A240V Europe 31 years 4 years (21) Necrotizing cellulitis; pathergy-like inflammation; pneumonia; lung abscesses None identified Minor trauma 
B.III.8 Male WT/p.E314X Middle East 6 years 1.5 years ​ Necrotizing cellulitis; skin abscesses; necrotizing panniculitis; pneumonia P. aeruginosa; Enterobacter spp. Vaccination 
C.II.3 Male WT/p.K247RfsX25 South America 16 years 0.5 years ​ Necrotizing cellulitis; skin abscesses; pyoderma gangrenosum; pneumonia P. aeruginosa; S. aureus; C. perfringens Vaccination; surgery 
D.II.3 Female WT/p.S351VfsX55 Europe 28 years 28 years ​ Necrotizing cellulitis; skin abscesses None identified Surgery 
E.II.8 Female WT/p.W148X Europe 41 years 15 years (22) Cellulitis; skin abscesses; chorioamnionitis; pyelonephritis Klebsiella spp.; Pseudomonas spp.; C. perfringens; E. coli Minor trauma 
F.II.3 Male WT/c.788G>A (predicted p.R263Q) North America 38 years 2 mo ​ Soft tissue abscesses; pyoderma gangrenosum; osteomyelitis; inflammatory bowel disease; pneumonia S. epidermidis Minor trauma; vaccination; surgery 

Patient characteristics and disease manifestations of the patients reported. WT, wild-type.

or Create an Account

Close Modal
Close Modal