Table 1.

Inborn errors of cytokines or their receptors, their corresponding autoimmune phenocopies (anti-cytokine auto-Abs), and monoclonal antibodies used in therapeutics, together with the associated infectious phenotypes

CytokineReceptor of cytokineInborn error of immunityMain infectious diseasePhenocopies (auto-Abs)Infectious diseaseTherapeutic with monoclonal AbsInfectious disease
Type II IFN (IFN-γ) IFNGR1
IFNGR2 
IFNG
IFNGR1
IFNGR2 
- Disseminated M. bovis–BCG disease
- Disseminated environmental mycobacteria disease 
Auto-Abs to IFN-γ - Disseminated environmental mycobacteria disease
- Disseminated tuberculosis
- Salmonellosis 
- Emapalumab
- Fontolizumab
- AMG811 
- Disseminated histoplasmosis
- Disseminated salmonellosis 
Type I IFNs (IFN-α/β) IFNAR1
IFNAR2 
IFNAR1
IFNAR2 
- Herpes virus encephalitis
- Severe influenza
- Yellow fever
- Life-threatening COVID-19 pneumonia 
Auto-Abs to IFN-α2, other IFN-α, IFN-β, IFN-ω - Life-threatening COVID-19 pneumonia
- Yellow fever vaccine disease 
- Sifalimumab/MEDI545
- Rontalizumab/RG-7415
- AGS-009
- S95021/19D11
-Anifrolimab/MEDI-546 
- Respiratory tract infections
- Herpes zoster 
IL-17A
IL-17F 
IL-17RA
IL-17RC 
IL17F
IL17RA
IL17RC 
Chronic mucocutaneous candidiasis Auto-Abs to IL-17A, IL-17F - Chronic mucocutaneous candidiasis - Secukinumab/AIN457
- Ixekizumab/LY2439821
- Brodalumab/AMG 827
- Bimekizumab 
- Chronic mucocutaneous candidiasis 
IL-6 IL-6R
GP130/IL6ST 
IL6R
IL6ST 
Staphylococcal cutaneous infections Auto-Abs to IL-6 - Staphylococcal cutaneous infections - Tocilizumab
- Sarilumab
- Satralizumab
- Sirukumab
- Siltuximab 
- Staphylococcal cellulitis
- Pneumonia by S. aureus 
GM-CSFa CSF2RA
CSF2RB 
CSF2RA
CSF2RB 
- Nocardiosis?
- Cryptococcosis? 
Auto-Abs to GM-CSF - Pulmonary and extra-pulmonary cryptococcosis
- Pulmonary and extra-pulmonary nocardiosis 
- Lenzilumab
- Namilumab
- Gimsilumab
- Otilimab
- Mavrilimumab 
- Nasopharyngitis without microbe isolation 
CytokineReceptor of cytokineInborn error of immunityMain infectious diseasePhenocopies (auto-Abs)Infectious diseaseTherapeutic with monoclonal AbsInfectious disease
Type II IFN (IFN-γ) IFNGR1
IFNGR2 
IFNG
IFNGR1
IFNGR2 
- Disseminated M. bovis–BCG disease
- Disseminated environmental mycobacteria disease 
Auto-Abs to IFN-γ - Disseminated environmental mycobacteria disease
- Disseminated tuberculosis
- Salmonellosis 
- Emapalumab
- Fontolizumab
- AMG811 
- Disseminated histoplasmosis
- Disseminated salmonellosis 
Type I IFNs (IFN-α/β) IFNAR1
IFNAR2 
IFNAR1
IFNAR2 
- Herpes virus encephalitis
- Severe influenza
- Yellow fever
- Life-threatening COVID-19 pneumonia 
Auto-Abs to IFN-α2, other IFN-α, IFN-β, IFN-ω - Life-threatening COVID-19 pneumonia
- Yellow fever vaccine disease 
- Sifalimumab/MEDI545
- Rontalizumab/RG-7415
- AGS-009
- S95021/19D11
-Anifrolimab/MEDI-546 
- Respiratory tract infections
- Herpes zoster 
IL-17A
IL-17F 
IL-17RA
IL-17RC 
IL17F
IL17RA
IL17RC 
Chronic mucocutaneous candidiasis Auto-Abs to IL-17A, IL-17F - Chronic mucocutaneous candidiasis - Secukinumab/AIN457
- Ixekizumab/LY2439821
- Brodalumab/AMG 827
- Bimekizumab 
- Chronic mucocutaneous candidiasis 
IL-6 IL-6R
GP130/IL6ST 
IL6R
IL6ST 
Staphylococcal cutaneous infections Auto-Abs to IL-6 - Staphylococcal cutaneous infections - Tocilizumab
- Sarilumab
- Satralizumab
- Sirukumab
- Siltuximab 
- Staphylococcal cellulitis
- Pneumonia by S. aureus 
GM-CSFa CSF2RA
CSF2RB 
CSF2RA
CSF2RB 
- Nocardiosis?
- Cryptococcosis? 
Auto-Abs to GM-CSF - Pulmonary and extra-pulmonary cryptococcosis
- Pulmonary and extra-pulmonary nocardiosis 
- Lenzilumab
- Namilumab
- Gimsilumab
- Otilimab
- Mavrilimumab 
- Nasopharyngitis without microbe isolation 
a

As explained in the text, inborn errors of and auto-Abs to GM-CSF underlie PAP. The infectious diseases seen in these patients are relatively diverse and may result from PAP (including its therapy) and/or from impaired GM-CSF–dependent immunity in alveolar macrophages.

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