Table 1.

Antagonist antibodies and drugs for immune inhibitory pathways and agonist antibodies for co-stimulatory receptors in clinical testing for cancer

Target Agent Company Indication Stage of Development 
Inhibitory pathway antagonists 
CTLA-4 Ipilimumab (αCTLA-4 Mab) Bristol-Myers Squibb Melanoma FDA approved 
   Multiple cancers Phase 1–3 
 Tremilimumab (αCTLA-4 Mab) MedImmune TBDb  
PD-1/PD-L1 MDX1106 (αPD-1 Mab) Bristol-Myers Squibb Melanoma, lung, kidney, etc. Phase 1–3 
 MK3475 (αPD-1 Mab) Merck Multiple cancers Phase 1 
 Amp224 (B7-DC-Ig) Amplimmune/GlaxoSmithKline Multiple cancers Phase 1 
 CT-011a (αPD-1) CureTech Multiple cancers Phase 1/2 
 MDX1105 (αPD-L1 Mab) Bristol-Myers Squibb Multiple cancers Phase 1 
B7-H3 MGA271 (αB7-H3 Mab) Macrogenics Multiple cancers Phase 1 
IDO D-1-methyl tryptophan NewLink Multiple cancers Phase 1/2 
Co-stimulatory pathway agonists 
CD137 BMS663513 (αCD137 Mab) Bristol-Myers Squibb TBDb  
CD40 CP-870893 (αCD40 Mab) Pfizer Pancreas cancer Phase 1 
OX40 Anti-OX40 Mab AgonOX Multiple cancers Phase 1/2 
CD127 CDX-1127 (αCD27 Mab) Celldex Multiple cancers Phase 1 
Target Agent Company Indication Stage of Development 
Inhibitory pathway antagonists 
CTLA-4 Ipilimumab (αCTLA-4 Mab) Bristol-Myers Squibb Melanoma FDA approved 
   Multiple cancers Phase 1–3 
 Tremilimumab (αCTLA-4 Mab) MedImmune TBDb  
PD-1/PD-L1 MDX1106 (αPD-1 Mab) Bristol-Myers Squibb Melanoma, lung, kidney, etc. Phase 1–3 
 MK3475 (αPD-1 Mab) Merck Multiple cancers Phase 1 
 Amp224 (B7-DC-Ig) Amplimmune/GlaxoSmithKline Multiple cancers Phase 1 
 CT-011a (αPD-1) CureTech Multiple cancers Phase 1/2 
 MDX1105 (αPD-L1 Mab) Bristol-Myers Squibb Multiple cancers Phase 1 
B7-H3 MGA271 (αB7-H3 Mab) Macrogenics Multiple cancers Phase 1 
IDO D-1-methyl tryptophan NewLink Multiple cancers Phase 1/2 
Co-stimulatory pathway agonists 
CD137 BMS663513 (αCD137 Mab) Bristol-Myers Squibb TBDb  
CD40 CP-870893 (αCD40 Mab) Pfizer Pancreas cancer Phase 1 
OX40 Anti-OX40 Mab AgonOX Multiple cancers Phase 1/2 
CD127 CDX-1127 (αCD27 Mab) Celldex Multiple cancers Phase 1 
a

Antibody not yet validated for target specificity.

b

Antibody previously tested in melanoma patients; plans to re-initiate clinical testing after a hiatus.

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