Table 1.
Microglial roles for AD risk genes identified in genome-wide associations
Gene/proteinMolecular functionActivities in microglial biology and AD
Lipid transport   
APOE Major apolipoprotein in brain HDL-like particles Conveys Aβ to lipoprotein receptors for clearance. Microglial Apoe expression induced in neurodegenerative models. 
CLU/apoJ Another apolipoprotein in brain, usually in separate lipoparticles from apoE Promotes Aβ solubility. Conveys Aβ to lipoprotein receptors for clearance (DeMattos et al., 2004). 
Transmembrane proteins   
SORL1 Receptor for vesicular sorting of lipoproteins and various receptors Binds Aβ and directs it to lysosome (Caglayan et al., 2014). Rare variant in this domain = familial AD. High microglial expression in human. 
ABCA7 ATP-binding cassette transporter; multipass transmembrane protein transports lipids Localizes to phagocytic cup (Jehle et al., 2006); presumed role in membrane remodeling. Impaired Aβ phagocytosis in Abca7-null mice (Fu et al., 2016). 
TREM2 Binds anionic/lipophilic ligands; triggers DAP12 ITAM to recruit kinase Syk Implicated in cell viability, chemotaxis, and phagocytosis. Disease mutations impair interactions with apoE and apoJ. 
CD33 Binds sialylated ligands; phosphorylated ITIM recruits phosphatase SHP-1 Protective allele reduces surface CD33 levels and enhances Aβ uptake. AD association not replicated in meta-analysis. 
MS4A6A Four-pass transmembrane protein in MS4A family; function unknown Likely involved in microglial receptor complex, like MS4A1 (CD20) in B cells and MS4A2 (FCER1B) in basophils/mast cells 
CR1 Complement receptor 1; binds C1q and C3b/C4b Recognizes opsonized targets. Inactivates C3b/C4b. Variant with extra C3b/C4b-binding domain increases AD risk (Brouwers et al., 2012). 
EPHA1 Receptor tyrosine kinase for ephrin-A class ligands Stimulates Pyk2 phosphorylation and migration in T lymphocytes (Aasheim et al., 2005). Not yet studied in microglia. 
HLA-DRB1/5 Major histocompatibility complex class II protein for extracellular antigen presentation May serve as intracellular adaptors during the innate immune response (Liu et al., 2011) 
IL1RAP Coreceptor with IL1R1 for IL-1 signaling Enables proinflammatory signal transduction that may mitigate plaque pathology but exacerbate Tau pathology (Ghosh et al., 2013) 
Membrane and cytoskeletal dynamics   
INPP5D/SHIP1 SH3-containing inositol phosphatase, converts phosphatidylinositol (3,4,5)-trisphosphate to phosphatidylinositol (3,4)-bisphosphate Interacts with DAP12, opposes PI3K recruitment, modulates receptor endocytosis, and curbs phagocytosis in macrophages 
PLCG2 Phospholipase activity cleaves phosphatidylinositol (4,5)-bisphosphate into IP3 and DAG second messengers Acts downstream of SYK during ITAM signaling. IP3 and DAG effect calcium and PKC signaling. 
CD2AP Adaptor protein between membrane proteins and actin cytoskeleton Interactions with SHIP1 and RIN3 (Bao et al., 2012; Rouka et al., 2015) suggest role in microglia endocytosis. Also implicated in neuronal APP trafficking and tau propagation. 
BIN1 Involved in membrane curvature and dynamin interaction RIN3 interaction (Kajiho et al., 2003) suggests role in microglia endocytosis. Also implicated in neuronal APP trafficking and tau propagation. 
RIN3-SLC24A4 RIN3: a guanine nucleotide exchange factor for Rab5 and Rab31 RIN3: interacts with BIN1 and CD2AP. Functions in the early endocytic pathway (Kajiho et al., 2011). 
PICALM Phosphatidylinositol-binding protein recruits clathrin and AP2 for vesicle assembly Possible role in microglial endocytosis. Also implicated in neuronal APP trafficking and Aβ efflux via blood–brain barrier transcytosis. 
PTK2B/Pyk2 Non–receptor tyrosine kinase; homologue of focal adhesion kinase Activated in microglia by fibrillar Aβ (Combs et al., 1999). Involved in chemotactic polarization and migration of macrophages (Okigaki et al., 2003). 
CASS4 Scaffold protein associated with focal adhesion kinases FAK, Pyk2 Largely unstudied. Functions inferred by homology with p130Cas family. 
ABI3 Component of the Abi/WAVE complex involved in actin polymerization (Sekino et al., 2015) Probably involved in microglial motility and/or phagocytosis 
FERMT2 Adaptor between membrane and actin cytoskeleton at extracellular matrix adhesion sites Not expressed in microglia; no conjectured role in microglial function. Implicated in APP trafficking. 
Transcription factors   
SPI1/PU.1 Important for myeloid and B cell lineages Originally identified SNP was intronic rs10838725 in CELF1 gene. Protective SPI1 SNP = reduced PU.1 levels. 
MEF2C Widely studied in muscle cells and neurons Microglial expression and calcium-dependent activation mechanisms (Lynch et al., 2005) suggest possible role downstream of TREM2. 
Other   
ZCWPW1 Presumed epigenetic regulator through its chromatin-binding domains SNPs across ∼10 genes show AD association; causal gene unknown. Neighboring genes encode paired immune receptors. 
NME8 Encodes protein with thioredoxin and nucleoside diphosphate kinase domains Unknown cellular function 
Gene/proteinMolecular functionActivities in microglial biology and AD
Lipid transport   
APOE Major apolipoprotein in brain HDL-like particles Conveys Aβ to lipoprotein receptors for clearance. Microglial Apoe expression induced in neurodegenerative models. 
CLU/apoJ Another apolipoprotein in brain, usually in separate lipoparticles from apoE Promotes Aβ solubility. Conveys Aβ to lipoprotein receptors for clearance (DeMattos et al., 2004). 
Transmembrane proteins   
SORL1 Receptor for vesicular sorting of lipoproteins and various receptors Binds Aβ and directs it to lysosome (Caglayan et al., 2014). Rare variant in this domain = familial AD. High microglial expression in human. 
ABCA7 ATP-binding cassette transporter; multipass transmembrane protein transports lipids Localizes to phagocytic cup (Jehle et al., 2006); presumed role in membrane remodeling. Impaired Aβ phagocytosis in Abca7-null mice (Fu et al., 2016). 
TREM2 Binds anionic/lipophilic ligands; triggers DAP12 ITAM to recruit kinase Syk Implicated in cell viability, chemotaxis, and phagocytosis. Disease mutations impair interactions with apoE and apoJ. 
CD33 Binds sialylated ligands; phosphorylated ITIM recruits phosphatase SHP-1 Protective allele reduces surface CD33 levels and enhances Aβ uptake. AD association not replicated in meta-analysis. 
MS4A6A Four-pass transmembrane protein in MS4A family; function unknown Likely involved in microglial receptor complex, like MS4A1 (CD20) in B cells and MS4A2 (FCER1B) in basophils/mast cells 
CR1 Complement receptor 1; binds C1q and C3b/C4b Recognizes opsonized targets. Inactivates C3b/C4b. Variant with extra C3b/C4b-binding domain increases AD risk (Brouwers et al., 2012). 
EPHA1 Receptor tyrosine kinase for ephrin-A class ligands Stimulates Pyk2 phosphorylation and migration in T lymphocytes (Aasheim et al., 2005). Not yet studied in microglia. 
HLA-DRB1/5 Major histocompatibility complex class II protein for extracellular antigen presentation May serve as intracellular adaptors during the innate immune response (Liu et al., 2011) 
IL1RAP Coreceptor with IL1R1 for IL-1 signaling Enables proinflammatory signal transduction that may mitigate plaque pathology but exacerbate Tau pathology (Ghosh et al., 2013) 
Membrane and cytoskeletal dynamics   
INPP5D/SHIP1 SH3-containing inositol phosphatase, converts phosphatidylinositol (3,4,5)-trisphosphate to phosphatidylinositol (3,4)-bisphosphate Interacts with DAP12, opposes PI3K recruitment, modulates receptor endocytosis, and curbs phagocytosis in macrophages 
PLCG2 Phospholipase activity cleaves phosphatidylinositol (4,5)-bisphosphate into IP3 and DAG second messengers Acts downstream of SYK during ITAM signaling. IP3 and DAG effect calcium and PKC signaling. 
CD2AP Adaptor protein between membrane proteins and actin cytoskeleton Interactions with SHIP1 and RIN3 (Bao et al., 2012; Rouka et al., 2015) suggest role in microglia endocytosis. Also implicated in neuronal APP trafficking and tau propagation. 
BIN1 Involved in membrane curvature and dynamin interaction RIN3 interaction (Kajiho et al., 2003) suggests role in microglia endocytosis. Also implicated in neuronal APP trafficking and tau propagation. 
RIN3-SLC24A4 RIN3: a guanine nucleotide exchange factor for Rab5 and Rab31 RIN3: interacts with BIN1 and CD2AP. Functions in the early endocytic pathway (Kajiho et al., 2011). 
PICALM Phosphatidylinositol-binding protein recruits clathrin and AP2 for vesicle assembly Possible role in microglial endocytosis. Also implicated in neuronal APP trafficking and Aβ efflux via blood–brain barrier transcytosis. 
PTK2B/Pyk2 Non–receptor tyrosine kinase; homologue of focal adhesion kinase Activated in microglia by fibrillar Aβ (Combs et al., 1999). Involved in chemotactic polarization and migration of macrophages (Okigaki et al., 2003). 
CASS4 Scaffold protein associated with focal adhesion kinases FAK, Pyk2 Largely unstudied. Functions inferred by homology with p130Cas family. 
ABI3 Component of the Abi/WAVE complex involved in actin polymerization (Sekino et al., 2015) Probably involved in microglial motility and/or phagocytosis 
FERMT2 Adaptor between membrane and actin cytoskeleton at extracellular matrix adhesion sites Not expressed in microglia; no conjectured role in microglial function. Implicated in APP trafficking. 
Transcription factors   
SPI1/PU.1 Important for myeloid and B cell lineages Originally identified SNP was intronic rs10838725 in CELF1 gene. Protective SPI1 SNP = reduced PU.1 levels. 
MEF2C Widely studied in muscle cells and neurons Microglial expression and calcium-dependent activation mechanisms (Lynch et al., 2005) suggest possible role downstream of TREM2. 
Other   
ZCWPW1 Presumed epigenetic regulator through its chromatin-binding domains SNPs across ∼10 genes show AD association; causal gene unknown. Neighboring genes encode paired immune receptors. 
NME8 Encodes protein with thioredoxin and nucleoside diphosphate kinase domains Unknown cellular function 

AD-associated genes are described in terms of microglial functions known or speculated to govern AD pathogenesis. References are provided only for certain material not mentioned elsewhere in the text.

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